RNA-guided genome editing à la carte
Two recent papers in Science illustrate how the prokaryotic CRISPR-Cas immune system machinery,which typically targets invasive genetic elements such as viruses and plasmids,can be converted into a sophisticated molecular tool for next-generation human genome editing.The versatile Cas9 RNA-guided endonuclease can be readily reprogrammed using customizable small RNAs for sequence-specific single-or double-stranded DNA cleavage.
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2013-07-29(万方平台首次上网日期,不代表论文的发表时间)
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733-734